Mild, moderate Gaucher Disease, Type 1
Drug | Drug Name | Drug Description |
---|---|---|
DB00419 | Miglustat | A glucosylceramide synthase inhibitor used for the management of mild to moderate type I Gaucher disease for patients who are not candidates for whole enzyme replacement. |
Drug | Drug Name | Target | Type |
---|---|---|---|
DB00419 | Miglustat | Ceramide glucosyltransferase | target |
Drug | Drug Name | Phase | Status | Count |
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